Міжн. реєстрація № 1499457
Поширити
Sarepta Therapeutics, Inc.
215 First Street
Cambridge MA 02142
(US)
Paul C. Llewellyn
ARNOLD & PORTER KAYE SCHOLER LLP
250 West 55th Street
New York NY 10019-9710
(US)
Англ.Pharmaceutical preparations for the treatment of neuromuscular diseases and disorders, muscular dystrophies, central nervous system diseases and disorders, genetic diseases and disorders; pharmaceutical preparations based on morpholino oligomer technology platform; pharmaceutical preparations that modulate rna expression; gene therapy products, namely, gene delivery pharmaceuticals; pharmaceutical preparations for gene therapy, gene editing, and genome editing; gene therapy products for the treatment of neuromuscular diseases and disorders, muscular dystrophies, central nervous system diseases and disorders, genetic diseases and disorders; biological preparations for the treatment of neuromuscular diseases and disorders, muscular dystrophies, central nervous system diseases and disorders, genetic diseases and disorders; viruses, viral vectors and viral constructs for the treatment of neuromuscular diseases and disorders, muscular dystrophies, central nervous system diseases and disorders, genetic diseases and disorders; pharmaceutical preparations, biological preparations and gene therapy products for the treatment of genetic disorders and diseases.